Vtesse VTS301 Study. Prospective, Randomized, Double-Blind, Sham-Controlled Trial of

Authors

Sameh Morkous MD, FAAN, Lehigh Valley Health NetworkFollow

Publication/Presentation Date

10-2015

Abstract

The purpose of this research study is to determine if a drug called 2-hydroxypropyl- β-cyclodextrin (VTS-270) will keep your child with NPC1 from getting sicker.

Comments

Study date: October 2015 - Present.

Published In/Presented At

Morkous, S. (2015). Vtesse VTS301 Study. Prospective, Randomized, Double-Blind, Sham-Controlled Trial of. LVHN Scholarly Works. Retrieved from https://scholarlyworks.lvhn.org/pediatrics/250

Disciplines

Medicine and Health Sciences | Pediatrics

Department(s)

Department of Pediatrics, Department of Pediatrics Faculty

Document Type

Research