Vtesse VTS301 Study. Prospective, Randomized, Double-Blind, Sham-Controlled Trial of
The purpose of this research study is to determine if a drug called 2-hydroxypropyl- β-cyclodextrin (VTS-270) will keep your child with NPC1 from getting sicker.
Published In/Presented At
Morkous, S. (2015). Vtesse VTS301 Study. Prospective, Randomized, Double-Blind, Sham-Controlled Trial of. LVHN Scholarly Works. Retrieved from http://scholarlyworks.lvhn.org/pediatrics/250
Medicine and Health Sciences | Pediatrics
Department of Pediatrics, Department of Pediatrics Faculty