X-linked retinoschisis: report of a family with a rare deletion in the XLRS1 gene.

Publication/Presentation Date

9-1-2003

Abstract

PURPOSE: To describe the clinical features and identify the disease causing mutation in a family with X-linked retinoschisis.

DESIGN: Cohort study.

METHODS: Genealogical investigation and mutation screening of the XLRS1 gene were performed in a four generation family of Icelandic ancestry. Three affected family members were evaluated clinically over a 29-year period.

RESULTS: A rarely reported, four base pair deletion (375- 378 del AGAT) in exon 5 of the XLRS1 gene was found in all affected males. A high degree of intrafamilial variability was observed in the progression of the disorder over 29 years.

CONCLUSIONS: Identification of the disease causing mutation in this family allows for the diagnosis of individuals at risk for this inherited macular degeneration. Furthermore, the long-term follow-up of subjects with identical mutations helps to better characterize the highly variable clinical course of this disorder.

Volume

136

Issue

3

First Page

547

Last Page

549

ISSN

0002-9394

Disciplines

Medicine and Health Sciences

PubMedID

12967815

Department(s)

Department of Medicine

Document Type

Article

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