Efficacy, safety and tolerability of chenodeoxycholic acid in adult patients with cerebrotendinous xanthomatosis (RESTORE): A randomized, placebo-controlled phase 3 stud
Publication/Presentation Date
2024
Volume
2
Issue
1
Published In/Presented At
Disciplines
Medicine and Health Sciences | Pediatrics
Department(s)
Department of Pediatrics
Document Type
Article
COinS