Treatment with Ataluren for Duchene Muscular Dystrophy
Publication/Presentation Date
12-4-2020
Abstract
Investigators from Europe and the USA, representing the STRIDE Registry and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS), examined the effectiveness of ataluren and standard of care in the Registry versus stand of care alone in the CINRG DNHS.
Volume
34
First Page
12
Last Page
12
ISSN
1043-3155
Published In/Presented At
Morkous S. S. (2020). Treatment with Ataluren for Duchene Muscular Dystrophy. Pediatric neurology briefs, 34, 12. https://doi.org/10.15844/pedneurbriefs-34-12
Disciplines
Medicine and Health Sciences | Pediatrics
PubMedID
33304086
Peer Reviewed for front end display
Peer-Reviewed
Department(s)
Department of Pediatrics, Department of Pediatrics Faculty
Document Type
Article
COinS