Title

Treatment with Ataluren for Duchene Muscular Dystrophy

Publication/Presentation Date

12-4-2020

Abstract

Investigators from Europe and the USA, representing the STRIDE Registry and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS), examined the effectiveness of ataluren and standard of care in the Registry versus stand of care alone in the CINRG DNHS.

Volume

34

First Page

12

Last Page

12

ISSN

1043-3155

Disciplines

Medicine and Health Sciences | Pediatrics

PubMedID

33304086

Peer Reviewed for front end display

Peer-Reviewed

Department(s)

Department of Pediatrics, Department of Pediatrics Faculty

Document Type

Article

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